Drug shrinks pediatric neural tumors
In an early-phase clinical trial, in most cases, children with neurofibromatosis type 1 and plexiform neurofibromas responded with tumor shrinkage.
Swedish teen walks using 3D printed hip implant
Fanny Fellesen, a Swedish 16-year-old with neurofibromatosis, was told she would never walk again.
Drug shows promise with hearing loss
A drug already in use for some cancers is not only halting hearing loss in some patients, but reversing it.
New drug approved for NF2 treatment
BioXcel announced the U.S. Food and Drug Administration has granted Orphan Drug Designation to BXCL101 for the treatment of Neurofibromatosis Type 2.